Migalastat (GR181413A) is an Orally Active and Competitive Inhibitor of α-Galactosidase A (α-Gal A)
Fabry disease is a rare lysosomal disorder characterized by deficient or absent α-galactosidase A (α-Gal A) activity resulting from mutations in the GLA gene. Migalastat is a pharmacological chaperone. It stabilizes…